Binding to a novel RNA-protein complex creates specificity for small molecule splicing modifiers to treat SMA

Sivaramakrishnan, M, McCarthy, KD, Huber, S, Campagne, S, Meier, S, Augustin, A, Heckel, T, Meistermann, H, Hug, M, Birrer, P, Moursy, A, Khawaja, S, Schmucki, R, Berntenis, N, Giroud, N, Golling, S, Tzouros, M, Banfai, B, Duran-Pacheco, G, Lamerz, J, Liu, YH, Luebbers, T, Ratni, H, Clery, A, Ebeling, M, Paushkin, S, Krainer, AR, Allain, F, Metzger, F (March 2017) Binding to a novel RNA-protein complex creates specificity for small molecule splicing modifiers to treat SMA. In: 10th Neuromuscular Translational Research Conference.

Item Type: Conference or Workshop Item (Paper)
Subjects: bioinformatics > genomics and proteomics > genetics & nucleic acid processing > DNA, RNA structure, function, modification > RNA splicing
diseases & disorders > congenital hereditary genetic diseases > spinal muscular atrophy
CSHL Authors:
Communities: CSHL labs > Krainer lab
SWORD Depositor: CSHL Elements
Depositing User: CSHL Elements
Date: March 2017
Date Deposited: 24 May 2021 13:34
Last Modified: 24 May 2021 13:34
Related URLs:
URI: https://repository.cshl.edu/id/eprint/40133

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